FDA Approves First Gene Therapy for Treatment of Aromatic L …
4 days ago · The U.S. Food and Drug Administration approved Kebilidi (eladocagene exuparvovec-tneq), an adeno-associated virus vector-based gene therapy indicated for the …
Gene Therapy News - ScienceDaily
5 days ago · Read all about gene therapy including current medical research on switching therapeutic genes on and off, light-activated gene therapy and gene silencing.
Gene therapy - Latest research and news | Nature
3 days ago · Gene therapy involves the introduction of new genes into cells, to restore or add gene expression, for the purpose of treating disease. Most commonly a mutated gene is …
FDA approves first gene-editing treatment for human illness
Dec 8, 2023 · In a landmark decision, the Food and Drug Administration Friday approved the first gene-editing treatment to alleviate human illness. The FDA approved two gene therapies for …
FDA Approves First Gene Therapies to Treat Patients with Sickle …
Today, the U.S. Food and Drug Administration approved two milestone treatments, Casgevy and Lyfgenia, representing the first cell-based gene therapies for the treatment of sickle cell disease...
FDA expands approval of first gene therapy for rare form of ... - CNN
Jun 20, 2024 · The US Food and Drug Administration has given the green light for the first gene therapy that treats a rare form of muscular dystrophy to be used in most people who have the …
FDA approves cure for sickle cell disease, the first ... - NBC News
Dec 8, 2023 · The FDA on Friday also approved a second treatment for sickle cell disease, called Lyfgenia, a gene therapy from drugmaker Bluebird Bio. Both treatments work by genetically …
FDA approves two gene therapies for sickle cell, bringing hope to ... - CNN
Dec 8, 2023 · The US Food and Drug Administration approved two gene-based treatments for sickle cell disease Friday, including the first therapy that uses the gene-editing technique …
Fresh from the biotech pipeline: record-breaking FDA approvals
Feb 26, 2024 · Nature Biotechnology - New drug approvals reached an all-time high in 2023, with five gene therapies, the first CRISPR–Cas9-edited therapy and a disease-modifying …
The world’s first CRISPR therapy is approved: who will ... - Nature
Nov 21, 2023 · The UK’s regulator has approved the world’s first CRISPR–Cas9 gene editing therapy, which aims to cure sickle cell disease and transfusion-dependent β-thalassemia.